CRISPR Cas9 AAVS1 Safe Harbor Knockin System
Efficient viral delivery of Cas9 into human safe harbor | Scientific Reports
AAVS1-EF1a
AAVS1-Targeted Plasmid Integration in AAV Producer Cell Lines | Human Gene Therapy Methods
Low-density lipoprotein receptor-deficient hepatocytes differentiated from induced pluripotent stem cells allow familial hypercholesterolemia modeling, CRISPR/Cas-mediated genetic correction, and productive hepatitis C virus infection | Stem Cell ...
Identification of the safe harbor locus, AAVS1, from porcine genome and site-specific integration of recombinase-mediated casset
Targeted transgene insertion into the AAVS1 locus driven by baculoviral vector‐mediated zinc finger nuclease expression in human‐induced pluripotent stem cells - Tay - 2013 - The Journal of Gene Medicine - Wiley Online Library
Efficient viral delivery of Cas9 into human safe harbor | Scientific Reports
Addgene: AAVS1-TetOn-3XFLAG-firefly-beta-globin-control-AAVS1 Sequences
Targeted Integration and High-Level Transgene Expression in AAVS1 Transgenic Mice after In Vivo HSC Transduction with HDAd5/35++ Vectors: Molecular Therapy
Engineering the AAVS1 locus for consistent and scalable transgene expression in human iPSCs and their differentiated derivatives - ScienceDirect
An AAVS1-Targeted Minigene Platform for Correction of iPSCs From All Five Types of Chronic Granulomatous Disease: Molecular Therapy
Addgene: AAVS1-EF1a-mTagRFP-T-CAAX
![PDF] Utilization of the AAVS1 safe harbor locus for hematopoietic specific transgene expression and gene knockdown in human ES cells. | Semantic Scholar](https://d3i71xaburhd42.cloudfront.net/69beb9bcd134cace2e02941831e199f56482e54d/3-Figure1-1.png "PDF] Utilization of the AAVS1 safe harbor locus for hematopoietic specific transgene expression and gene knockdown in human ES cells. | Semantic Scholar")
PDF] Utilization of the AAVS1 safe harbor locus for hematopoietic specific transgene expression and gene knockdown in human ES cells. | Semantic Scholar
Inserting an expression cassette into the AAVS1 locus in hiPS cells
Site-specific integration of adeno-associated virus involves partial duplication of the target locus | PNAS
Addgene: pJT039 AAVS1 -PuroR-9xTet0-pEF-IGKleader-hIgG1_FC-Myc-PDGFRb-T2A-Citrine-PolyA
Safe harbor-targeted CRISPR-Cas9 homology-independent targeted integration for multimodality reporter gene-based cell tracking | Science Advances
Characterization of the Mouse Adeno-Associated Virus AAVS1 Ortholog | Journal of Virology
Addgene: AAVS1-Puro-CAG-GCaMP6s
SplitAx: A novel method to assess the function of engineered nucleases | PLOS ONE
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Addgene: AAVS1-idCas9-vpr
Human AAVS1 safe harbor gene knock-in kits | Genecopoeia
Genome-TALER™ & Genome-CRISPR™ Human AAVS1 Safe Harbor Gene Knock-in Kit
Inserting an expression cassette into the AAVS1 locus in hiPS cells
Quantification of transgene expression in GSH AAVS1 with a novel CRISPR/Cas9-based approach reveals high transcriptional variation: Molecular Therapy - Methods & Clinical Development
